Atamyo Therapeutics and the EIC Accelerator: Gene Therapy for LGMD

30 September 2026920 words5 min

Atamyo Therapeutics, founded in 2020 as the first gene therapy spin-off of Genethon, the French gene therapy research centre in Évry, develops one-time gene therapies for limb-girdle muscular dystrophies (LGMD), rare inherited diseases that waste the muscles of the hips and shoulders. It was co-founded by chief executive Stéphane Degove and Isabelle Richard, a CNRS research director who heads Genethon's muscular dystrophy laboratory, according to Atamyo. The EIC selected its ATA-100 programme, a "smart, organotropic gene therapy" for LGMD-R9, for blended finance at the March 2024 cut-off. CORDIS lists no project for this award, and Atamyo's news pages do not mention it, so the grant amount, dates and deliverables are not public.

ATA-100 delivers a working copy of the FKRP gene, whose mutations cause LGMD-R9, which affects about 5,000 people in the US and Europe, the company says. In April 2025 Atamyo completed the dose-finding part of its Phase 1b/2b trial: two doses in two cohorts of three patients each, with no safety concerns according to an independent monitoring board, according to Atamyo. In the lower-dose cohort, all functional and tissue measures improved in all three patients; for the higher dose, "the same level of efficacy was not observed so far". The lower dose was chosen for the pivotal phase. ATA-100 also received a US Rare Pediatric Disease Designation.

6Patients in ATA-100 dose-finding
+19%Walking speed, lower dose, 12 months
4Patients dosed with ATA-200
NoneEIC project record on CORDIS

Company file

Legal entity
Atamyo Therapeutics SAS, SIREN 891 260 978, Évry-Courcouronnes
Founded
November 2020, spin-off of Genethon
Co-founders
Stéphane Degove (CEO), Isabelle Richard (CSO)
Lead programmes
ATA-100 (LGMD-R9), ATA-200 (LGMD-R5)
Designations
Orphan drug (US, EU), Fast Track and Rare Pediatric Disease (US) for ATA-100
Public funding
Bpifrance deeptech aid, €2M (2022)
EIC funding
Blended finance, amount not published

Where Atamyo Stands Now

Atamyo's second programme, ATA-200 for LGMD-R5, is in a single-centre trial at the University of Florida funded with the Dion Foundation. Four patients have been dosed, and 12-month data from the first two showed safety and "promising efficacy", according to Atamyo in May 2026. The ATA-100 trial record lists six enrolled patients and "active, not recruiting", according to ClinicalTrials.gov; no start of the pivotal part has been announced. The French register puts its workforce at three to five employees, and its accounts are not in the public INPI dataset.

The record

Two gene therapies for rare muscle diseases

Atamyo finished the dose-finding part of its ATA-100 trial in 2025. CORDIS lists no project for its March 2024 EIC award.

  1. Nov 2020Company foundedGenethon spin-off, Évry
  2. Feb 2022Bpifrance €2MDeeptech aid for ATA-100 trial
  3. Sep 2022ATA-100 trial startsLGMD-R9, Europe
  4. Mar 2024EIC Accelerator cut-offATA-100blended finance
  5. Feb 2025ATA-200 trial startsLGMD-R5, University of Florida
  6. Apr 2025ATA-100 dose-finding completeLower dose selected
  7. May 2026ATA-200 data at ASGCTFour patients dosed

Atamyo Therapeutics, ClinicalTrials.gov and the French business register.

"ATA-100 is the first treatment in LGMD-2i/R9 to present improvements in all functional endpoints in all patients treated."

Stéphane Degove, CEO and co-founder of Atamyo, April 2025

The Technology: Replacing a Missing Muscle Gene

Atamyo's therapies use an adeno-associated virus to carry a healthy gene into muscle. The EIC award describes ATA-100 as "organotropic", designed to target the right tissues for efficacy, safety and affordability. In muscle biopsies, the company reports increased glycosylation of alpha-dystroglycan, the protein chemistry that faulty FKRP disrupts.

The results

ATA-100 first dose cohort at 12 months

In three patients on the lower dose, breathing capacity, walking speed and quality-of-life scores improved on average. The higher dose did not show the same effect so far.

Atamyo Therapeutics, April 2025. Average improvement, per cent.

What the EIC Award Promised, and What the Record Shows

Without a CORDIS record or a company announcement, the EIC project's scope and status cannot be checked. The award title matches ATA-100's development. The public record shows the dose-finding phase completed with three responders on the chosen dose, which is a small base, and no pivotal-phase start two and a half years after the award.

  1. Dose-finding completeDeliveredApril 2025.
  2. Pivotal phase startedNot announcedTrial not recruiting.
  3. Detailed results publishedConferencesNo paper found.
  4. EIC project on recordMissingNot on CORDIS.

The evidence base

Patients treated in Atamyo's trials

The ATA-100 dose-finding study treated six patients in two cohorts; the ATA-200 trial has dosed four.

ClinicalTrials.gov and Atamyo Therapeutics. Patients.

The Money

Atamyo's disclosed public funding includes €2 million of Bpifrance deeptech aid in 2022 for the first ATA-100 trial, according to Atamyo. The ATA-200 trial is backed by the Dion Foundation. No equity round, EIC grant payment or EIC Fund investment has been announced.

What Cannot Be Checked

Questions for the EIC

Whether Atamyo signed the EIC grant agreement, how much it received, whether the EIC Fund invested, how the pivotal ATA-100 phase is funded and when it will start are not public.

Why Europe Should Care

There is no curative treatment for LGMD-R9, the company notes. Atamyo turns more than 25 years of LGMD research at Genethon into clinical candidates. Its next step, a pivotal trial, is the most expensive one.

What the award promised

A smart, affordable gene therapy for LGMD-R9.

What the record shows

Encouraging six-patient results, no pivotal start, no EIC project record.

The Verdict

Early promise, no public project record

Atamyo's science shows signals in tiny trials. What the EIC funded is not on the public record.

Atamyo Therapeutics and the EIC have not been asked for comment for this article. It is based entirely on public records and published statements, linked throughout.

Industry

HealthBiopharmaceuticals

Focus
  • Gene therapies
Technologies
  • Viral vectors
Keywords
  • Limb-girdle muscular dystrophy
  • Adeno-associated virus
  • Rare diseases
  • Orphan drugs